Earlier this year, Gallaudet University established a Gene Editing Think Tank, building on years of sustained conversation, ...
The ethics of using safe gene therapies to improve the health and cognition of Down syndrome children and adults.
Many new gene therapy treatments aren’t as profitable as predicted. But the reasons why don’t quite fit Goldman Sachs’ ...
UniQure will seek UK marketing authorization for its Huntington’s disease gene therapy AMT-130 in Q3 2026 after favorable talks with the UK regulator. The company is also preparing for a U.S. FDA ...
You might like the sound of this news. In a landmark move, the Food and Drug Administration on Thursday approved the first ...
At a first meeting on pediatric gene and cell therapy trials, participants discussed when enrolling children before adults is ethical and when to wait.
It's really hard to draw some arbitrary line in the sand. I do wonder if there was much debate back in the day about man-made antibiotics. It's very much in line with antivax thinking. I feel like ...
UniQure Gene Therapy’s Clinical Trial Results Keep It on Path to Become First Huntington’s Treatment
A uniQure gene therapy slowed progression of Huntington’s disease by 75% after three years, statistically significant clinical trial results the company says will support plans for a regulatory ...
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have ...
The US Food and Drug Administration on Thursday approved the first gene therapy for inherited hearing loss, a one-time ...
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